The tyrosinemia type 1 treatment is expected to grow at a CAGR of 6.50% during the forecast period of 2025-2034 driven by increasing awareness of the condition across the 8 major markets.
Base Year
Historical Year
Forecast Year
Increasing awareness and advancements in diagnostic technologies are enabling earlier detection of tyrosinemia type 1, driving demand for effective treatments and boosting market growth.
In June 2022, Nitisinone tablets received regulatory approval, reflecting a supportive environment for drug development. This approval enhances treatment accessibility, positively influencing the treatment market landscape positively.
The United States will likely dominate the market in the forecast period. This can be attributed to key players seeking regulatory approvals and robust healthcare infrastructure in the region.
Tyrosinemia type 1 is a rare genetic disorder caused by the inability to break down tyrosine, leading to severe liver and kidney complications. The market is driven by advancements in diagnostic technologies and increased awareness. Several market trends such as regulatory approvals and rising demand for innovative therapies impact the market significantly, leading to global market expansion.
Efforts to Enhance Early Diagnosis to Drive the Market Growth
Tyrosinemia type 1, a rare genetic disorder affecting males and females equally, has a global prevalence of approximately 1 in 100,000 to 120,000 births. Increasing awareness and advancements in diagnostic technologies are enabling earlier detection, while the growing demand for innovative treatment options supports market expansion. These factors, combined with improving healthcare infrastructure, are creating significant opportunities for the development and boosting the market value for innovative treatment alternatives.
Several trends and developments are being observed in the market to enhance the current situation. Some of the noteworthy trends are as follows.
The market report offers a detailed analysis of the market based on the following segments:
Market Breakup by Drug
Market Breakup by Dosage Form
Market Breakup by Distribution Channel
Market Breakup by Region
Market Share Based on Dosage Form to Witness Substantial Growth
Based on dosage form, the market is divided into tablets, capsules, and others. Among these, the capsule segment is expected to dominate the market share, due to its several advantages such as the ease of swallowing and masking the unpleasant taste and odor of the medications. For instance, in February 2024, Eton Pharmaceuticals officially introduced Nitisinone capsules for the management of tyrosinemia type 1. This medication is distributed through specialized pharmacies and is intended to be used alongside a stringent diet that restricts tyrosine and phenylalanine intake.
Based on region, the market report covers the United States, United Kingdom, Germany, France, Italy, Spain, Japan, and India. Among these, the United States is expected to account for a substantial market share due to the key market players seeking expedited regulatory approvals to manage the disease effectively. In addition, favorable reimbursement policies and robust healthcare infrastructure further support market growth in the region.
The key features of the market report include patent analysis, clinical trials analysis, grants analysis, funding and investment analysis, and strategic initiatives by the leading players. The major companies are:
Established in 2017 and headquartered in Deer Park, Illinois, Eton Pharmaceuticals focuses on developing treatments for rare diseases. The company offers ALKINDI SPRINKLE and Betaine Anhydrous, targeting metabolic disorders, including tyrosinemia type 1. Eton is dedicated to improving treatment accessibility for patients with unique therapeutic needs.
Founded in 2001, Sobi is headquartered in Stockholm, Sweden. The company specializes in rare disease therapies and has a focus on innovative solutions for addressing the unmet needs of patients with rare metabolic disorders. Their products include Nitisinone, a key treatment for Tyrosinemia type 1.
Rare Disease Therapeutics, established in 1991 and headquartered in Franklin, Tennessee, focuses on orphan drug development. The company provides Orfadin (Nitisinone) for treating tyrosinemia type 1, ensuring effective care for patients. RDT is committed to advancing treatments for rare and ultra-rare diseases.
Founded in 1926 and headquartered in Milan, Italy, Recordati Rare Diseases develops therapies for rare conditions. The company offers Nitisinone, addressing tyrosinemia type 1. With a strong commitment to innovation, Recordati continues to enhance its portfolio for rare metabolic disorder treatments.
*Please note that this is only a partial list; the complete list of key players is available in the full report. Additionally, the list of key players can be customized to better suit your needs.*
Other companies include WEP Clinical, Torrent Pharma Inc., and Nobelpharma Co., Ltd., among others.
*While we strive to always give you current and accurate information, the numbers depicted on the website are indicative and may differ from the actual numbers in the main report. At Expert Market Research, we aim to bring you the latest insights and trends in the market. Using our analyses and forecasts, stakeholders can understand the market dynamics, navigate challenges, and capitalize on opportunities to make data-driven strategic decisions.*
Get in touch with us for a customized solution tailored to your unique requirements and save upto 35%!
Explore our key highlights of the report and gain a concise overview of key findings, trends, and actionable insights that will empower your strategic decisions.
| REPORT FEATURES | DETAILS |
| Base Year | 2024 |
| Historical Period | 2018-2024 |
| Forecast Period | 2025-2034 |
| Scope of the Report |
Historical and Forecast Trends, Industry Drivers and Constraints, Historical and Forecast Market Analysis by Segment:
|
| Breakup by Drug |
|
| Breakup by Dosage Form |
|
| Breakup by Distribution Channel |
|
| Breakup by Region |
|
| Market Dynamics |
|
| Supplier Landscape |
|
| Companies Covered |
|
Datasheet
One User
USD 3,299
USD 2,969
tax inclusive*
Single User License
One User
USD 5,499
USD 4,969
tax inclusive*
Five User License
Five User
USD 6,999
USD 5,949
tax inclusive*
Corporate License
Unlimited Users
USD 8,199
USD 6,969
tax inclusive*
*Please note that the prices mentioned below are starting prices for each bundle type. Kindly contact our team for further details.*
Flash Bundle
Small Business Bundle
Growth Bundle
Enterprise Bundle
*Please note that the prices mentioned below are starting prices for each bundle type. Kindly contact our team for further details.*
Flash Bundle
Number of Reports: 3
20%
tax inclusive*
Small Business Bundle
Number of Reports: 5
25%
tax inclusive*
Growth Bundle
Number of Reports: 8
30%
tax inclusive*
Enterprise Bundle
Number of Reports: 10
35%
tax inclusive*
How To Order
Our step-by-step guide will help you select, purchase, and access your reports swiftly, ensuring you get the information that drives your decisions, right when you need it.
Select License Type
Choose the right license for your needs and access rights.
Click on ‘Buy Now’
Add the report to your cart with one click and proceed to register.
Select Mode of Payment
Choose a payment option for a secure checkout. You will be redirected accordingly.
Track prices with detailed trend reports.
Analyse trade data for supply chain insights.
Leverage cost reports for smart savings
Enhance supply chain with partnerships.
Gain insights to stay ahead and seize opportunities.
Get insights & trends for a competitive edge.
Track prices with detailed trend reports.
Analyse trade data for supply chain insights.
Leverage cost reports for smart savings
Enhance supply chain with partnerships.
Gain insights to stay ahead and seize opportunities.
Get insights & trends for a competitive edge.
Track prices with detailed trend reports.
Analyse trade data for supply chain insights.
Connect For More Information
Our expert team of analysts will offer full support and resolve any queries regarding the report, before and after the purchase.
Our expert team of analysts will offer full support and resolve any queries regarding the report, before and after the purchase.
We employ meticulous research methods, blending advanced analytics and expert insights to deliver accurate, actionable industry intelligence, staying ahead of competitors.
Our skilled analysts offer unparalleled competitive advantage with detailed insights on current and emerging markets, ensuring your strategic edge.
We offer an in-depth yet simplified presentation of industry insights and analysis to meet your specific requirements effectively.
Australia
63 Fiona Drive, Tamworth, NSW
+61-448-061-727
India
C130 Sector 2 Noida, Uttar Pradesh 201301
+91-723-689-1189
Philippines
40th Floor, PBCom Tower, 6795 Ayala Avenue Cor V.A Rufino St. Makati City,1226.
+63-287-899-028, +63-967-048-3306
United Kingdom
6 Gardner Place, Becketts Close, Feltham TW14 0BX, Greater London
+44-753-713-2163
United States
30 North Gould Street, Sheridan, WY 82801
+1-415-325-5166
Vietnam
193/26/4 St.no.6, Ward Binh Hung Hoa, Binh Tan District, Ho Chi Minh City
+84-865-399-124
United States (Head Office)
30 North Gould Street, Sheridan, WY 82801
+1-415-325-5166
Australia
63 Fiona Drive, Tamworth, NSW
+61-448-061-727
India
C130 Sector 2 Noida, Uttar Pradesh 201301
+91-723-689-1189
Philippines
40th Floor, PBCom Tower, 6795 Ayala Avenue Cor V.A Rufino St. Makati City, 1226.
+63-287-899-028, +63-967-048-3306
United Kingdom
6 Gardner Place, Becketts Close, Feltham TW14 0BX, Greater London
+44-753-713-2163
Vietnam
193/26/4 St.no.6, Ward Binh Hung Hoa, Binh Tan District, Ho Chi Minh City
+84-865-399-124
Share